| (210) | Number of the EPO application | 17783207 |
| (220) | Filing date of the EPO application | 2017.04.14 |
| (80) | EPO patent specification publication (B) | EPB nr. 11/2024, 2024.03.13 |
| (110) | EPO patent number | 3442600 |
| (21) | Number of the application | e 2019 0235 |
| (71) | Name(s) of applicant(s), code of the country | RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL, US; |
| (72) | Name(s) of inventor(s), code of the country | RODINO-KLAPAC Louise, US;
MENDELL Jerry R., US; |
| (73) | Name(s) of owner(s), code of the country | RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL, US; |
| (54) | Title of the invention | ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF B-SARCOGLYCAN AND MICRORNA-29 AND THE TREATMENT OF MUSCULAR DYSTROPHY |
| (13) | Kind-of-document code | A1 |
| (51) | International Patent Classification | A61K 48/00 (2006.01.01); A61P 21/00 (2006.01.01); C07K 14/47 (2006.01.01); C12N 15/12 (2006.01.01); C12N 15/85 (2006.01.01) |
| (19) | Country | US |
| (41) | Date of publication of the application | 2019.03.31 |
| (30) | Priority | 201662323333 P, 2016.04.15, US; 201662433548 P, 2016.12.13, US |
| (86) | International application | PCT/US2017/027583, 2017.04.14 |
| (87) | International publication | WO 2017/180976, 2017.10.19 |